Vol. 46 (3) 2025 Neuro endocrinology letters

Clinical and Genetic Spectrum of Titinopathy: A Turkish Pediatric Case Series.

OBJECTIVES: Our aim is to contribute to the literature by presenting pediatric titinopathy cases with different clinical and genetic profiles, including the newly identified homozygous TTN mutation. METHODS: We retrospectively evaluated five pediatric patients with genetically confirmed titinopathy who presented to the Cukur.....